Whats Happening

What's happening in the fight to cure Sanfilippo?

"The first patient has been treated with a new, experimental gene therapy, and the next child will be enrolled soon."

Glenn O'Neill, father or Eliza

Exciting progress is being made.

The Sanfilippo community is pleased to see several potential therapies moving towards human trial. In addition to clinical stage programs, there are several early stage innovative approaches being developed. Check back soon for updates.


We are pleased to announce that Glenn O’Neill has assumed the position of our Executive Director. Glenn co-founded our Foundation three years ago and has since led it in a volunteer capacity, helping to shape who we are we today. Read the press release.

Information about global research

For information about research beyond those funded by the Cure Sanfilippo Foundation, visit these links:

How we push for progress

To learn more about how we are working to make and fund progress in the effort to cure Sanfilippo, visit our What We Do page.

Cure Sanfilippo Foundation

501c3 non-profit
(Tax ID: 46-4322131)


P.O. Box 6901
Columbia, SC 29260